This Week In Huntington's Disease Research keeps you up-to-date on HDSA research activities, recently published work about Huntington’s disease, historical moments in HD research and more.

PRECISION-HD2 Results from Wave Life Sciences Expected in Late 2019

Posted on August 1, 2019

Wave Life Sciences is conducting two early safety studies of huntingtin-lowering therapies, called PRECISION-HD1 and PRECISION-HD2. In a business update…

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HD Legacy: Brain Donation for HD Research

Posted on July 25, 2019

To enable cutting-edge Huntington’s disease research, HDSA is collaborating with CHDI to support the donation of brain and other organs…

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Gene Silencing Therapy for Amyloidosis Approved in the UK

Posted on July 17, 2019

Last week saw the approval of a genetic therapy for a rare disease called hereditary transthyretin-mediated amyloidosis (hATTR amyloidosis). As…

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The Blog Returns: 34th Annual HDSA Convention Research Recap

Posted on July 11, 2019

This week, Dr. Fox returns from maternity leave and resumes the HDSA research blog! The 34th Annual HDSA Convention in…

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#LetsTalkAboutHD

Posted on April 4, 2019

May is HD awareness month, and every day HDSA will be sharing family stories, celebrity PSAs, HD facts and much…

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Roche/Genentech Amends GENERATION-HD1 Study

Posted on March 28, 2019

On Thursday, March 21st, Roche/Genentech released a Community Statement about changes to the GENERATION-HD1 study, the clinical trial testing huntingtin-lowering…

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Interview with Roche Representatives

Posted on March 21, 2019

A few weeks ago we blogged about the Annual CHDI Huntington’s disease Therapeutics Conference in Palm Springs, California. This week,…

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Gene Therapy 101

Posted on March 14, 2019

In addition to ongoing clinical trials of Roche/Genentech and Wave huntingtin-lowering therapies, a number of other companies are developing drugs…

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Annual CHDI Huntington’s Disease Therapeutics Conference

Posted on March 7, 2019

This week in Palm Springs, California, CHDI Foundation hosted the 14th Annual HD Therapeutics Conference. This yearly conference draws academic…

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Second Annual HD-COPE Meeting

Posted on February 28, 2019

The Huntington’s Disease Coalition for Patient Engagement (HD-COPE) met this week in New York City. HD-COPE unites organizations serving HD…

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HDSA Research Webinar on DNA Repair Next Thursday, February 20th

Posted on February 14, 2019

Over the past 15-20 years we have learned that the CAG repeat mutation that causes HD is dynamic – the…

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HDSA Expands Centers of Excellence Program to 47 Sites

Posted on February 7, 2019

HDSA Centers of Excellence provide world-class multidisciplinary care to families all over the United States. Professionals at these locations include…

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First Patient Enrolled in Pivotal Huntingtin-Lowering Trial

Posted on January 31, 2019

This week, Ionis Pharmaceuticals issued a press release stating that the Phase 3 trial of the huntingtin-lowering therapy formerly known…

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Two Announcements From Drug Companies

Posted on January 24, 2019

This week, we learned that the SIGNAL trial has completed recruitment for its Phase 2 study of VX15/2503 (pepinemab), a…

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2018 Research Year In Review Webinar Available

Posted on January 17, 2019

If you weren’t able to join us for the 2018 HD Research Year-in-Review webinar or would like to have another…

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American Society of Human Genetics Chooses Huntington’s Disease as Topic for 2019 Essay Contest

Posted on January 10, 2019

The American Society of Human Genetics (ASHG) is a nonprofit organization whose mission is to advance human genetics in science,…

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2018 Research Year in Review Webinar

Posted on January 3, 2019

To complement our 2018 Research Report, George and Leora will be sharing this year’s HD research highlights in our 2018…

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