This Week In Huntington's Disease Research keeps you up-to-date on HDSA research activities, recently published work about Huntington’s disease, historical moments in HD research and more.

First Gene-Silencing Drug Approved by the FDA

Posted on August 16, 2018

This week marked the first FDA approval of a gene silencing drug, for a rare hereditary disease called ATTR amyloidosis….

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Roche Huntingtin-Lowering Drug Gains PRIME Status from EMA

Posted on August 7, 2018

On August 4th, Roche Pharmaceuticals announced that their huntingtin-lowering therapy was granted PRIME status from the European Medicines Agency (EMA)….

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Voice Your Opinions About The Future Of CRISPR

Posted on August 2, 2018

Community research surveys are valuable ways for researchers to get input from HD patients, families and caregivers about a variety…

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At-Home DNA Kits Require Caution

Posted on July 26, 2018

At-home DNA kits like 23 & Me are growing in popularity, and claim to provide information about your health and…

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Pipeline of Therapies for HD

Posted on July 19, 2018

The Rare Disease Report covers stories about medicine, finance, and advocacy in rare disease fields. Last week an article explored…

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DNA Repair Research Uncovers New Drug Targets

Posted on July 12, 2018

Researchers led by Ray Truant at McMaster University in Canada are investigating how DNA repair could help correct some of…

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Research Highlights from the 33rd Annual HDSA Convention

Posted on July 5, 2018

As we ease into the summer, enjoy some highlights from our research sessions at HDSA’s 33rd Annual Convention in Los…

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HDSA’s 33rd Annual Convention Research Forum Video Now Available

Posted on June 14, 2018

HDSA’s 33rd Annual Convention in Los Angeles from June 7th-9th included the 2018 Research Forum, where ten speakers collaborated to tell…

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HDSA Convention Research Forum

Posted on June 7, 2018

This week we’re hosting the 33rd Annual HDSA Convention in Los Angeles, California. Tune in to the livestream of our Research Forum…

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Huntington’s Disease Featured in Nature Outlook

Posted on May 31, 2018

The prestigious journal Nature publishes both research reports and journalistic articles, and is widely read by scientists and non-scientists. This…

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Participate in a Research Study at the HDSA Convention

Posted on May 24, 2018

If you are negative for the HD gene, currently participate in Enroll-HD, and will be attending HDSA’s Convention in June,…

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HDSA Announces 2018 Berman-Topper HD Career Development Fellowship Recipient

Posted on May 17, 2018

The 2018 HDSA Berman-Topper fellowship has been awarded to Dr. Rachel Harding for her proposal entitled “Structural and biophysical investigations…

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May is HD Awareness Month

Posted on May 10, 2018

Join the #HDSAFamily as we turn up the global volume on HD awareness. Visit for more info. Don’t forget…

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Positive Trends in Data from Ionis Huntingtin-Lowering Trial

Posted on May 3, 2018

On April 24th, 2018, Ionis Pharmaceuticals made an announcement about the Phase 1/2 clinical trial of their huntingtin-lowering drug, IONIS-HTTRx…

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Ionis/Roche Present Trial Data at World’s Largest Neurology Conference

Posted on April 26, 2018

Huntington’s disease was featured this week at the American Academy of Neurology (AAN) Conference, where 12,000 medical professionals gathered for…

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Appreciating Research Volunteers

Posted on April 19, 2018

This week HDSA is celebrating National Volunteer Appreciation Week. This goes for research, too! We’d like to express our heartfelt…

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Research Forum at HDSA’s 33rd Annual Convention

Posted on April 12, 2018

Huntington’s disease research plays a big role at our annual Convention, which is taking place this year on June 7th-9th…

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Interview Study for Parents and Adolescents about Genetic Risk

Posted on April 5, 2018

If you are 15-17 years old or are the parent of a 15-17 year old, consider participating in an interview…

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HDSA’s Human Biology Project

Posted on March 29, 2018

The identification of the HD gene led to the development of many animal models that have helped us to better…

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25th Anniversary of Discovering the HD gene

Posted on March 22, 2018

This week marks 25 years since the identification of the gene that causes Huntington’s disease. The discovery of the repeating…

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