It was a pleasure to see so many faces, familiar and new, in Atlanta for the 37th Annual HDSA Convention,…
Researchers in Spain are studying whether a combination of vitamins approved to treat a different brain disorder, biotin-thiamine responsive basal ganglia…
A study recently published in Nature detailed scientists’ understanding of how branaplam, a drug originally developed for treatment of spinal muscular atrophy…
For the first time in two years, scientists, clinicians, and industry partners convened in Palm Springs, CA for CHDI foundation’s 17th Annual HD Therapeutics Conference….
CHDI is a privately funded HD research foundation whose mission is to further development of HD therapies. This week, they’re hosting…
When you have a rare disease, you face two battles – one being the illness itself, and the other, living…
Researchers at UCLA have developed a new mouse model for HD that more closely resembles human HD than ever before….
Huntingtin lowering (HTT-lowering) has been touted as a promising avenue for treatment of HD because it targets the cause of…
Researchers with PTC Therapeutics recently published exciting new findings – a promising new huntingtin lowering drug that can be taken…
Novartis is developing an experimental HD therapy called branaplam which has the potential to lower huntingtin when taken by mouth. Branaplam…
In a press release published this morning, uniQure announced that AMT-130, an investigational gene therapy for treatment of Huntington’s disease,…
A research team led by Dr. Celia Dominguez at CHDI has identified a new method to track the presence of…
Earlier this week on November 16, HDSA launched applications for the 2022 cycles of its prestigious Berman-Topper Family HD Career…
In September, the European Huntington’s Disease Network brought together scientists and stakeholders from around the world for updates from experts in…
In a recent press release, Prilenia Therapeutics and the Huntington’s Study Group (HSG) announced the completion of participant enrollment in PROOF-HD,…
The editors of HD Buzz recently sat down with leaders from Roche to ask questions on behalf of the HD community…
After an unexpected dosing halt in the GENERATION-HD1 study nearly 6 months ago, Roche is gearing up to increase their…
Researchers at the Children’s Hospital of Philadelphia have created a system to better regulate gene editing by administration of a secondary activator drug. This novel system, dubbed Xon, acts…
A new system has been developed that allows researchers to fine-tune gene expression with oral drugs, work that provides a…
The August 9th press release from Voyager Therapeutics left many of us scratching our heads. Luckily, HDBuzz swooped in with their latest…