Summary
- Applications open for the HDSA Berman-Topper and Donald King Fellowships
- uniQure shares positive data from their ongoing gene therapy study
- Roche issues community letter
- At-home interview for people who have had psychotherapy
Applications open for the HDSA Berman-Topper and Donald King Fellowships
HDSA has launched applications for the 2024 cycles of its competitive Berman-Topper Family HD Career Development Fellowship (for postdocs) and Donald A. King Summer Research Fellowship (for undergrads). To learn more about these exciting opportunities and how to apply, visit the Berman-Topper Fellowship and Donald A. King Fellowship pages on HDSA’s website.
uniQure shares positive data from their ongoing gene therapy study
On December 19th uniQure issued a press release and held a video conference to share the latest data from their ongoing study of AMT-130, an experimental gene therapy being developed for HD. This investigational huntingtin-lowering gene therapy is delivered once via brain surgery and delivers a new set of genetic instructions that tell the body to intercept and destroy the message to make huntingtin protein. Data up to 30 months showed a strong safety profile and potentially some stabilization of HD symptoms. Although the study was designed to test safety and not efficacy, it’s a very promising sign that we will see further development of AMT-130 moving forward. You can check out the press release here. The presentation was targeted at investors but can be accessed publicly here. And HDBuzz talked about the news and what it means in their latest article.
Roche issues community letter
Roche has shared an end-of-year community letter that talks about the progress of the GENERATION HD2 study of tominersen and the recent publication of GENERATION HD1 results. HD families are essential to their ongoing research efforts. Check out the letter here.
At-home interview for people who have had psychotherapy
Researchers at The University of Reading (UK) would like people living with Huntington’s Disease (HD) who have had experience with psychological therapy (whether successful or unsuccessful) to come forward and talk about their experience. If you are living at risk of Huntington’s, are presymptomatic or symptomatic, and have engaged with psychological therapy with a psychologist, you may be eligible to participate. The researchers are conducting interviews to gather different experiences and learn from participant insights what is and isn’t helpful in psychological therapy practice. If you have any experience with psychological therapy, are over the age of 18, have access to a computer and can speak and understand the English language, you may be eligible to participate. Please contact the researcher to arrange a convenient time to talk at g.r.adams@reading.ac.uk.
